Small Molecule Therapy for Genetic Disease / 
Edited by Jess G. Thoene. 
 - 1 online resource (238 pages) :  digital, PDF file(s). 
<br/><br/> Title from publisher's bibliographic system (viewed on 28 Apr 2015). 
<br/><br/><label>ISBN: </label>9780511777905 (ebook) 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Metabolism, Inborn errors of--Chemotherapy--Handbooks, manuals, etc.<br/>Metabolism, Inborn errors of--Gene therapy--Handbooks, manuals, etc.<br/>Genetic disorders--Chemotherapy--Handbooks, manuals, etc.<br/>Genetic Diseases, Inborn--drug therapy.<br/>Orphan Drug Production.<br/>Rare Diseases--drug therapy.<br/>Small Molecule Libraries--therapeutic use.